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Technology3h 10m ago

RAG-17 siRNA therapy demonstrated 69% SOD1 knockdown in a first-in-human ALS trial.

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Who
RAG-17
What
RAG-17 siRNA therapy demonstrated 69% SOD1 knockdown in a first-in-human ALS trial.
When
Thu, 16 Jul 2026 16:23:51 GMT · 3h 10m ago
Where
Not specified ·
Why
To test the efficacy of RAG-17 siRNA therapy in reducing SOD1 levels in ALS patients.
The Frontline Impact

How this affects you

The trial results suggest a potential advancement in gene silencing therapies for ALS, reshaping expectations for the durability of gene silencing.

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